Asfotase Alfa for Treating Paediatric Onset Hypophosphatasia (PP156) (PDF, 284Kb)
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Burosumab for Treating X-linked Hypophosphataemia in Children and Young People, Policy Position (PP177), May 2019.pdf (PDF, 557Kb)
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Canakinumab for treating periodic fever syndromes: TRAPS, HIDS/MKD and FMF (ages 2 and older), Policy Position Statement, (PP228). January 2022. (PDF, 324Kb)
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National Acute Porphyria, Service Specification (CP166). February 2019 (PDF, 274Kb)
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PP155 Pasireotide for Cushing's Disease (PDF, 252Kb)
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PP187 Treatment Options for Transthyretin Amyloidosis in Adults (PDF, 389Kb)
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